uniQure N.V.

Products

Category Product Brand Description
Global Market for Cell and Gene Therapy (BIO225B)
Hemgenix (etranacogene dezaparvovec)
The FDA approved Hemgenix (etranacogene dezaparvovec) as the first gene therapy for hemophilia B and UniQure's second internally developed gene therapy to receive approval. In February 2023, Hemgenix received conditional marketing authorization (CMA) from the EC, making it the first one-time gene therapy for hemophilia in the EU.

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