Lysosomal Disease Treatments: Technologies and Global Markets

Report Code: PHM183A

Publish Date: Oct 2018

Publisher: BCC Publishing

Category: Pharmaceuticals

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Report Highlights

The global market for lysosomal storage diseases treatment should grow from $5.1 billion in 2018 to reach $7.6 billion by 2023 at a compound annual growth rate (CAGR) of 8.3% for the period of 2018-2023.

Report Includes 

  • 37 data tables and 25 additional tables
  • An overview of the global market for lysosomal disease treatments
  • Analyses of global market trends, with data from 2017, estimates for 2018 and projections of compound annual growth rates (CAGRs) through 2023
  • Segmentation of the global market by cancer therapy indiscation, treatment type, route of administration, end-use, application and geographical region
  • Information on current regulatory environment, and a trend analysis of recent government policies and regulations for lysosomal disease treatments
  • Assessment of lysosomal storage diseases by the accumulated substrate and the profitability of focusing on ultra-orphan diseases
  • Profiles of major players in the industry, including Astellas Pharma, Astrazeneca, Eli Lilly and Co., Merck & Co., Inc., and Novo Nordisk A/S

Report Scope

The lysosomal storage disease treatment market has been divided by type of indication into: Gaucher’s Diseases, Fabry Diseases, Pompe’s Syndrome, Mucopolysaccharidosis and more. Mucopolysaccharidosis is further segmented into Hunter syndrome, Hurlers Syndrome and Moriquo syndrome. The market is also segmented by routing of administration into IV and oral. The market has been divided into hospitals, clinics and other facilities into end users by type of treatment into enzyme replacement therapy and substrate reduction therapy. The market has been segmented into North America, Europe, Asia-Pacific and RoW.

Analyst Credentials

Neha Maliwal is a graduate in biotechnology with an MBA in Marketing from Pune University in India. With more than five years of experience in the market research industry, she has worked as a business analyst across various industries, such as healthcare IT and the U.S. mortgage industry. She has authored many BCC Research reports, with topics including healthcare analytics, antibiotics and sample preparation.

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Table of Contents

All reports provided in PDF format. For shared licensing options (5+ Users), please call a representative at (+1) 781-489-7301 or contact us at info@bccresearch.com
Title/Chapter NamePagesMember Price
Full Report: Lysosomal Disease Treatments: Technologies and Global Markets118Free
Chapter- 1: Introduction5Free
Chapter- 2: Summary and Highlights3Free
Chapter- 3: Market Overview and Background23Free
Chapter- 4: Treatment Options for Lysosomal Storage Diseases7Free
Chapter- 5: Market Breakdown by Disease Type21Free
Chapter- 6: Market Breakdown by Route of Administration3Free
Chapter- 7: Market Breakdown by End Use3Free
Chapter- 8: Market Breakdown by Treatment Type4Free
Chapter- 9: Market Breakdown by Region14Free
Chapter- 10: Company Profiles24Free
Chapter- 11: Appendix A: Global List of Lysosomal Storage Disease Societies2Free
Chapter- 12: Appendix B: Abbreviations1Free
Chapter- 13: Appendix C: Glossary of Terms8Free

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This is an Excel-only version of the report.

Report Includes

    Total Number of Tables in this Report: 62

  • Summary Table: Global Market for Lysosomal Storage Diseases Treatment, by Type, Through 2023
  • Table 1: Major Events in Lysosomal Storage Diseases, 1882-2004
  • Table 2: Types of Lysosomal Storage Diseases
  • Table 3: Most Common LSDs
  • Table 4: Orphan Drug Regulations in Different Countries
  • Table 5: Comparison of Policies in Different Countries
  • Table 6: Orphan Drug Market Exclusivity in Various Countries
  • Table 7: Summary of Selective LSDs Intended for Newborn Screening, Clinical and Biochemistry Features and Comparison of Enzyme Methods
  • Table 8: Recommendations to Overcome the Restraints
  • Table 9: Therapeutic Options and Target Diseases
  • Table 10: Global Market for Gaucher’s Disease Treatment, by Region, Through 2023
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Lysosomal Disease Treatments: Technologies and Global Markets
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